India Orphan Diseases Drugs Market Analysis

India Orphan Diseases Drugs Market Analysis

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The India Orphan Diseases Drugs Market is projected to grow from $2.815 Bn in 2022 to $7.645 Bn by 2030, registering a CAGR of 13.30% during the forecast period of 2022 - 2030. The lack of attention and funding for research and treatment of these diseases has led to limited options for patients. However, recent efforts by the government and healthcare organizations are increasing awareness and access to care for those affected by orphan diseases in India. Some of the key players in the India orphan diseases drugs market include Roche, Novartis, Pfizer, Sanofi, AstraZeneca, GlaxoSmithKline, Merck, AbbVie, Johnson & Johnson, and Takeda.

ID: IN10INPH019 CATEGORY: Pharmaceuticals GEOGRAPHY: India AUTHOR: Shivam Zalke

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India Orphan Diseases Drugs Market Executive Summary

The India Orphan Diseases Drugs Market is projected to grow from $2.815 Bn in 2022 to $7.645 Bn by 2030, registering a CAGR of 13.30% during the forecast period of 2022 - 2030.

The orphan diseases drugs market in India is growing due to increasing awareness, better access to healthcare, and government support. However, the market faces challenges such as limited patient populations, high costs of treatments, and limited reimbursement options. Despite these challenges, the market is expected to continue growing due to increasing demand for treatments and government efforts to support the development of drugs for orphan diseases.

Orphan diseases in India are rare and debilitating conditions that affect a small number of people. Some of the most common orphan diseases in India include thalassemia, sickle cell anemia, and inherited metabolic disorders. The lack of attention and funding for research and treatment of these diseases has led to limited options for patients. However, recent efforts by the government and healthcare organizations are increasing awareness and access to care for those affected by orphan diseases in India.

india orphan diseases drugs market analysis

Market Dynamics

Market Drivers

The key drivers of the India orphan diseases drugs market are:

  1. Growing patient population: The number of people affected by orphan diseases in India is increasing, driving demand for treatments
  2. Improving healthcare access: Improved access to healthcare and increased spending on healthcare are contributing to the growth of the market
  3. Government support: The Indian government has implemented policies to support the development and approval of drugs to treat orphan diseases
  4. Increasing awareness: Increased public and government awareness of the burden of orphan diseases is driving demand for treatments
  5. Advances in technology: Advances in technology and research are leading to the development of new treatments for orphan diseases

Competitive Landscape

Key Players

Some of the key players in the India orphan diseases drugs market include:

  • Roche
  • Novartis
  • Pfizer
  • Sanofi
  • AstraZeneca
  • GlaxoSmithKline
  • Merck
  • AbbVie
  • Johnson & Johnson
  • Takeda

These companies are involved in the research, development, and commercialization of drugs to treat orphan diseases in India and around the world.

Healthcare Policies and Regulatory Landscape

The Indian government has implemented several policies to support the development and approval of drugs to treat orphan diseases, including:

Orphan Drug Designation: The Central Drugs Standard Control Organization (CDSCO) has established a system for granting orphan drug designation to drugs intended to treat rare diseases. This designation provides benefits such as expedited regulatory review and marketing exclusivity.

Research and Development Funding: The government provides funding for the research and development of treatments for orphan diseases through various programs and initiatives.

Reimbursement Policies: The government has implemented reimbursement policies to ensure that patients have access to treatments for orphan diseases, but these policies are limited in scope and coverage.

The CDSCO is the main regulatory body responsible for the approval of drugs to treat orphan diseases in India. The agency has established a streamlined review process for orphan drugs to expedite their approval and availability to patients. The regulatory landscape for the India orphan diseases drugs market is constantly evolving, and companies must stay informed of changes to ensure compliance with regulatory requirements.

1. Executive Summary
1.1 Disease Overview
1.2 Global Scenario
1.3 Country Overview
1.4 Healthcare Scenario in Country
1.5 Patient Journey
1.6 Health Insurance Coverage in Country
1.7 Active Pharmaceutical Ingredient (API)
1.8 Recent Developments in the Country

2. Market Size and Forecasting
2.1 Epidemiology of Disease
2.2 Market Size (With Excel & Methodology)
2.3 Market Segmentation (Check all Segments in Segmentation Section)

3. Market Dynamics
3.1 Market Drivers
3.2 Market Restraints

4. Competitive Landscape
4.1 Major Market Share

4.2 Key Company Profile (Check all Companies in the Summary Section)

4.2.1 Company Overview Product Applications and Services Recent Developments Partnerships Ecosystem Financials (Based on Availability)

5. Reimbursement Scenario
5.1 Reimbursement Regulation
5.2 Reimbursement Process for Diagnosis
5.3 Reimbursement Process for Treatment

6. Methodology and Scope

Orphan Diseases Drugs Market Segmentation

Therapeutic area

  • Cancer
  • Neurological condition
  • Cardiovascular condition
  • Musculoskeletal condition
  • Hematologic condition
  • Others

Route of administration

The injectable segment dominated the market and is expected to witness significant growth during the forecast period. This can be attributed to the launch of novel injectables for the treatment of rare diseases.

  • Oral
  • Injectable
  • Others

Drug Type

Biologics dominated the market and is expected to witness significant growth during the forecast period. The advancement in biotechnology and research techniques has facilitated the development of novel biologics. High target specificity and potential of biological drugs revolutionizing the treatments of several rare diseases are expected to fuel the segment growth.

  • Biologics
  • Biosimilars  
  • Small molecule

Distribution Channel

The specialty pharmacy segment dominated the market. The dominance can be attributed to strategic initiatives undertaken by key players, such as the acquisition of specialty pharmacies for the distribution of their products.

  • Hospital Pharmacy
  • Specialty Pharmacy
  • Online Pharmacy

Insights10 will provide you with the reports within 10 key parameters which are:

  1. Market Overview
  2. Market Growth Drivers & Restraints
  3. Epidemiology of Disease Type
  4. Market Segmentation
  5. Market Share
  6. Competitive Landscape
  7. Key Company Profiles
  8. Healthcare Policies & Regulatory Framework
  9. Reimbursement Scenario
  10. Factors Driving Future Growth

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Last updated on: 03 February 2023
Updated by: Shivam Zalke

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