India Fabry Disease Drugs Market Analysis

India Fabry Disease Drugs Market Analysis


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India Fabry disease drugs market is projected to grow from $xx Mn in 2023 to $xx Mn by 2030, registering a CAGR of xx% during the forecast period of 2023 - 2030. The market for fabry disease drugs is growing rapidly as a result of increase in incidence and prevalence of fabry disease globally, increase in awareness about the disease globally, better diagnosis rates, improved access to treatment, development of new emerging therapies, orphan drug designations provided by regulatory body?s, increase in stratergic collaborations, rise in research and development activities and approval of promising pipeline products. Chiesi Farmaceutici SpA , Sanofi, Shire ,Takeda Pharmaceutical Company Limited, Amicus Therapeutics, Inc., JCR Pharmaceuticals, Moderna are the key market players operating in global fabry disease drugs market.

ID: IN10INRD084 CATEGORY: Rare Diseases GEOGRAPHY: India AUTHOR: Sakshi Mantri

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India Fabry Disease Drugs Market Analysis Summary

India Fabry Disease Drugs Market is valued at around $20.55 Mn in 2022 and is projected to reach $45.03 Mn by 2030, exhibiting a CAGR of 10.3% during the forecast period 2023-2030.

Fabry disease is a rare X-chromosome-linked genetic disease which is caused by deficient activity of a lysosomal enzyme called α-galactosidase. This results in the dysfunction of glycosphingolipid (fat) metabolism. α-galactosidase enzyme is responsible for breaking down complex sugar-lipid molecules called glycolipids or digesting particular compounds. The deficiency of this enzyme may result in cell abnormalities and organ system dysfunction which is caused by an abnormal buildup of a specific fatty matter called globotriaosylceramide in multiple tissues of the body including eyes, skin, kidney, gastrointestinal system, brain, heart, and central nervous system. Since there is no known cure for Fabry's disease, treatment options often focus on managing difficulties brought on by the disease's development and relieving symptoms. Current treatments include enzyme replacement therapy (ERT), chaperone treatment, and substrate reduction therapy (SRT). Development in oral chaperone therapy is taking place which is projected to drive the market in future years. The popularity of substrate reduction therapies and gene therapies in the market is also expected to increase.

Market Dynamics

Market Drivers

Increase in incidence and prevalence of Fabry disease – As the patient population suffering from this disease increase this acts as a market growth driver.

An increase in awareness about the disease globally is a market growth driver

The increase in the prevalence and adoption of novel therapies like chaperone treatment, substrate therapy and gene therapy acts as a market growth driver. Chaperone therapy includes oral small molecules, which aim to stabilize and enhance the function of the deficient enzyme.

Extensive research and development activities and collaborations between pharmaceutical companies and research organizations also act as market growth drivers.

Orphan Drug Designations provided by regulatory bodies also act as a growth driver.

Market Restraints

Side effects associated with treatment options and high treatment costs act as a market growth restraint

A lower rate of diagnosis due to a lack of technologies and the late onset of symptoms also acts as a market growth restraint.

Key players

Genzyme (Sanofi) Amicus Therapeutics Inc. Pfizer Inc. Sanofi Shire plc BioMarin Pharmaceutical Inc. Catalyst Biosciences Inc. uniQure N.V. Orchard Therapeutics plc Alnylam Pharmaceuticals Inc.

1. Executive Summary
1.1 Disease Overview
1.2 Global Scenario
1.3 Country Overview
1.4 Healthcare Scenario in Country
1.5 Patient Journey
1.6 Health Insurance Coverage in Country
1.7 Active Pharmaceutical Ingredient (API)
1.8 Recent Developments in the Country

2. Market Size and Forecasting
2.1 Epidemiology of Disease
2.2 Market Size (With Excel & Methodology)
2.3 Market Segmentation (Check all Segments in Segmentation Section)

3. Market Dynamics
3.1 Market Drivers
3.2 Market Restraints

4. Competitive Landscape
4.1 Major Market Share

4.2 Key Company Profile (Check all Companies in the Summary Section)

4.2.1 Company
4.2.1.1 Overview
4.2.1.2 Product Applications and Services
4.2.1.3 Recent Developments
4.2.1.4 Partnerships Ecosystem
4.2.1.5 Financials (Based on Availability)

5. Reimbursement Scenario
5.1 Reimbursement Regulation
5.2 Reimbursement Process for Diagnosis
5.3 Reimbursement Process for Treatment

6. Methodology and Scope

Market Segmentations For India Fabry disease drugs market

By Type

  • Classic Fabry disease 
  • Atypical late-onset Fabry disease

By Treatment type

  • Enzyme replacement therapy (ERT)
  • Chaperone treatment
  • Substrate reduction therapy (SRT)
  • Others

By Mechanism of action

  • Alpha-galactosidase A (Alpha-Gal A) agonist
  • Globotriaosylceramide (GL-3) deposition reducer
  • Pancreatic replacement enzymes
  • Pain management 
  • Others

By Route of Administration

  • Oral
  • Parenteral

By end users

  • Hospitals
  • Homecare
  • Speciality clinics
  • Others

Insights10 will provide you with the reports within 10 key parameters which are:

  1. Market Overview
  2. Market Growth Drivers & Restraints
  3. Epidemiology of Disease Type
  4. Market Segmentation
  5. Market Share
  6. Competitive Landscape
  7. Key Company Profiles
  8. Healthcare Policies & Regulatory Framework
  9. Reimbursement Scenario
  10. Factors Driving Future Growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision-making for business stakeholders. Our focused approach to developing reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

 

Stage I: Market Data Collection

Primary Interviews: We have developed a network of experts, freelancers, and researchers across countries through which we engage with local experts to gather key data points and assumptions about each market. We also engage regularly with some of the best market research agencies such as Atheneum, GuidePoint, GLG, etc. to conduct surveys and interviews, and build intelligence. We have language translators as a part of our team, who between them can cover 30+ languages allowing us to extract better local insights.

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Data Sources: We have access to multiple highly reliable free and subscription data sources. We have many years of experience to understand which sources are more dependable for what and which to prefer for the reliable and latest information. The key sources of information include the following, but are not limited to:

 

 

Stage II: Market Data Analysis and Statistical Model

Market Trends: We generally look at macro parameters and micro indicators. The macro parameters include changes in government policies, demand and supply of the market, government intervention programs, and major market share. The micro indicators are GDP growth, market size, market volume, etc. We also understand nuances specific to each country like the US, Canada, India, Germany, etc., and have worked across 60+ countries and hence not only understand global trends but how these differ by country, how payment models, market structure, cultural parameters, etc. differ in each country.

Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. starting with the large overall market and segmenting different areas and the bottom-up approach i.e. starting with population and epidemiology and rolling up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach is mainly used for new product forecasting and the bottom-up approach is used for demand estimation of any product for different countries summed up to form the total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as Asia-Pacific, Africa, Europe, Middle East, North America, and  Latin America for the period of 2022 to 2030. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape, and policy and regulatory scenario, and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

Data triangulation of various sources and results of the research are carried out by benchmarking with reliable sources such as industry statistics, statistical databases, and company-level averages, etc.

We make sure to finalize the numbers in alignment with the market research. Firstly, our internal experts ensure thorough validation and checking to ensure accurate and precise analysis and then validation is also done using a multiple-data analysis model. Two-level validation is done and entails the finalization of the report scope and the way of representation pattern.

 

 

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analyzed and synthesized. The second series of interviews are done if necessary to check and validate. The future opportunities are analyzed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results is then, interpreted by considering the following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing the regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue/volume
  • ​Analyzing current needs and determining penetration to estimate the market

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Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

Presentation & Reporting: The market research report is presented in different forms such as charts by using a scientific approach for easy understanding. Historic, current, and future analysis is provided for each market in terms of both value and volume. The size of the market is interpreted in the US Dollar value and the respective unit, based on the product, for volume consumption.

The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

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Last updated on: 04 July 2023
Updated by: Shivam Zalke

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