Canada Pyruvate Kinase (PK) Deficiency Market Analysis

Canada Pyruvate Kinase (PK) Deficiency Market Analysis


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Canada Pyruvate Kinase (PK) deficiency market is projected to grow from $xx Mn in 2023 to $xx Mn by 2030, registering a CAGR of xx% during the forecast period of 2023 - 2030. The market for Pyruvate Kinase (PK) deficiency is growing rapidly as a result of increase in incidence and prevalence of disease, increased awareness about the disease, improved diagnostic techniques, advancements in treatment options, increase in research and development and rise in patient assistance programmes. Agios pharmaceuticals, Pfizer Inc., Sanofi, Novartis, Teva Pharmaceutical Industries Ltd, Green cross corporation are the top key market players operating in the global Pyruvate Kinase (PK) deficiency market.

ID: IN10CARD108 CATEGORY: Rare Diseases GEOGRAPHY: Canada AUTHOR: Gaurav Bhongale

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Canada Pyruvate Kinase (PK) Deficiency Market Analysis Summary

Canada Pyruvate Kinase (PK) Deficiency Market is valued at around $43.4 Mn in 2022 and is projected to reach $75.7 Mn by 2030, exhibiting a CAGR of 7.2% during the forecast period 2023-2030.

Pyruvate kinase deficiency is a rare genetic disorder in which deficiency of the enzyme pyruvate kinase occurs which is essential for the process of producing energy in red blood cells. The main cause for PK deficiency is autosomal recessive trait that is the child gets the disease from their family members. Hemolytic anaemia, a disorder brought on by this deficiency, is a condition where red blood cells live a shorter life. The severity of PK Deficiency can vary greatly from person to person, and the symptoms might appear at various ages. Fatigue and weakness, pale skin (pallor), shortness of breath, rapid heart rate, yellowing of the skin and eyes (jaundice), enlargement of the spleen, and gallstones are the common symptoms of this disease. Blood transfusion, bone marrow transplantation, splenectomy, phototherapy, folic acid supplementation, vitamin B supplementation, iron chelation (key-lay-shun), cholecystectomy and allogeneic hematopoietic stem cell transplantation (HSCT) are the different treatment options available. The main goal of treatment for PK Deficiency is to manage the symptoms and complications associated with the condition. Momenta Pharmaceuticals, Inc, Apellis Pharmaceuticals, F. Hoffmann-La Roche Ltd, Teva Pharmaceutical Industries Ltd, Zydus Cadila, Vertice Pharma, Concord Biotech, Alkem Labs, Dr. Reddy’s Laboratories Ltd, Jubilant Life Sciences Ltd, Strides Pharma Science Limited, Mylan N.V., Novartis AG, Sanofi, Rigel Pharmaceuticals Inc, Incyte Corporation, Alexion Pharmaceuticals are the top key global market players.

Market Dynamics

Market Drivers

An increase in the incidence and prevalence of disease, increased awareness about the disease, improved diagnostic techniques, advancements in treatment options, increase in research and development and rise in patient assistance and advocacy programmes are the main market growth drivers.

Market Restraints

Expensive treatment costs and a lack of skilled professionals are market growth restraints.

Key players

Alexion Pharmaceuticals Grifols Kedrion Biopharma Octapharma Baxter International Takeda Pharmaceutical Company Pfizer Sanofi BioMarin Pharmaceutical Novartis

1. Executive Summary
1.1 Disease Overview
1.2 Global Scenario
1.3 Country Overview
1.4 Healthcare Scenario in Country
1.5 Patient Journey
1.6 Health Insurance Coverage in Country
1.7 Active Pharmaceutical Ingredient (API)
1.8 Recent Developments in the Country

2. Market Size and Forecasting
2.1 Epidemiology of Disease
2.2 Market Size (With Excel & Methodology)
2.3 Market Segmentation (Check all Segments in Segmentation Section)

3. Market Dynamics
3.1 Market Drivers
3.2 Market Restraints

4. Competitive Landscape
4.1 Major Market Share

4.2 Key Company Profile (Check all Companies in the Summary Section)

4.2.1 Company
4.2.1.1 Overview
4.2.1.2 Product Applications and Services
4.2.1.3 Recent Developments
4.2.1.4 Partnerships Ecosystem
4.2.1.5 Financials (Based on Availability)

5. Reimbursement Scenario
5.1 Reimbursement Regulation
5.2 Reimbursement Process for Diagnosis
5.3 Reimbursement Process for Treatment

6. Methodology and Scope

Market Segmentations For Canada Pyruvate Kinase (PK) Deficiency market

By Population

  • Infants
  • Children
  • Adults

By Diagnosis

  • Bilirubin in the blood
  • Complete blood count (CBC), 
  • Genetic testing
  • Haptoglobin blood test
  • Osmotic fragility
  • Pyruvate kinase activity
  • Stool urobilinogen

By treatment

  • Blood transfusion
  • Bone marrow transplantation
  • Splenectomy
  • Phototherapy
  • Folic acid and vitamin B supplementation
  • Iron chelation (key-lay-shun)
  • Cholecystectomy
  • Allogeneic hematopoietic stem cell transplantation (HSCT)

By Distribution Channels:

  • Hospital pharmacies
  • Retail pharmacies
  • Online pharmacies
  • Others

By end users

  • hospitals
  • Research organizations
  • Clinics
  • Others

Insights10 will provide you with the reports within 10 key parameters which are:

  1. Market Overview
  2. Market Growth Drivers & Restraints
  3. Epidemiology of Disease Type
  4. Market Segmentation
  5. Market Share
  6. Competitive Landscape
  7. Key Company Profiles
  8. Healthcare Policies & Regulatory Framework
  9. Reimbursement Scenario
  10. Factors Driving Future Growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision-making for business stakeholders. Our focused approach to developing reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

 

Stage I: Market Data Collection

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Stage II: Market Data Analysis and Statistical Model

Market Trends: We generally look at macro parameters and micro indicators. The macro parameters include changes in government policies, demand and supply of the market, government intervention programs, and major market share. The micro indicators are GDP growth, market size, market volume, etc. We also understand nuances specific to each country like the US, Canada, India, Germany, etc., and have worked across 60+ countries and hence not only understand global trends but how these differ by country, how payment models, market structure, cultural parameters, etc. differ in each country.

Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. starting with the large overall market and segmenting different areas and the bottom-up approach i.e. starting with population and epidemiology and rolling up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach is mainly used for new product forecasting and the bottom-up approach is used for demand estimation of any product for different countries summed up to form the total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as Asia-Pacific, Africa, Europe, Middle East, North America, and  Latin America for the period of 2022 to 2030. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape, and policy and regulatory scenario, and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

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We make sure to finalize the numbers in alignment with the market research. Firstly, our internal experts ensure thorough validation and checking to ensure accurate and precise analysis and then validation is also done using a multiple-data analysis model. Two-level validation is done and entails the finalization of the report scope and the way of representation pattern.

 

 

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analyzed and synthesized. The second series of interviews are done if necessary to check and validate. The future opportunities are analyzed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results is then, interpreted by considering the following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing the regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue/volume
  • ​Analyzing current needs and determining penetration to estimate the market

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Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

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The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

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Last updated on: 04 July 2023
Updated by: Vidhi Upadhyay

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